The PubMed bibliographic database gives scientific results from all the teams working on SANFILIPPO syndrome throughout the world.

All articles on Mucopolysaccharidosis type III (sorted by date, newest first)

We have sorted this scientific literature into therapeutic avenues, with the following links:

Substrate reduction therapy

Enzyme replacement therapy

Molecular chaperones

Stop-codon read-through

Gene therapy

Cell therapy

Links to scientific literature according to enzyme deficiency: (search on the article title)

type IIIA

type IIIB

type IIIC

type IIID